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+====== HIBM Sialic Acid Trial Recruitment ======
+{{:ux001_cl101_phase_1_online_ad_w_irb_changes_2011jul20_2_.jpg?200 |}}
+**Ultragenyx Pharmaceutical Announces the Start of a Phase 1 Clinical Trial for Hereditary Inclusion Body Myopathy (HIBM) - also known as Nonaka Myopathy or Distal Myopathy with Rimmed Vacuoles (DMRV)**
+(Novato, CA, July 20, 2011) -- Ultragenyx Pharmaceutical has announced that recruitment has begun for a first clinical study for HIBM patients.  To be eligible, patients need to have their HIBM diagnosis confirmed with a genetic test.   This first study is a short study to see how the investigational drug circulates in the body.
+“People with this rare disorder previously had no compelling reason to undergo genetic testing to understand their genetic mutation or to obtain a definitive diagnosis,” said Emil Kakkis, MD, PhD, President and CEO of Ultragenyx.  “As clinical trials are initiated patients will need a documented diagnosis of HIBM to be eligible, so we are helping them to get genetic testing.”
+To obtain testing at no cost, patients should contact their doctor and ask them to order sample collection kits from Ultragenyx for testing.
+* * * *
+Contacts: \\
+To order test collection kit; John Ditton\\
+jditton@ultragenyx.com  \\
+To learn more about the Clinical Trials; Mari Maurer, RN, BSN\\ mmaurer@ultragenyx.com  \\
+Phase 1 Trial Site Contacts: \\
+Clinilabs, Inc.\\
+-994-4567\\
+W. 55th Street, 4th Floor\\
+New York, NY 10019\\
+participate@clinilabs.com \\
+www.clinilabs.com\\
+West Coast Clinical Trials\\
+-668-1500 ext 4009\\
+Howard Way, Suite 100\\
+Costa Mesa, Ca. 92626\\
+ptinfo@wcct.com\\
+www.wcct.com\\
+**Ultragenyx PDF Press Release** \\
+{{:ux001_cl101_phase_1_online_ad_w_irb_changes_2011jul20_2_.pdf|}}
+\\ \\